PrincetonOne Delivers Top Talent for Novel Gene Therapy Launch in Rare Disease Space
Our Partner A biotechnology company focused on developing and commercializing genetic medicines for patients with rare diseases through gene therapy. Challenge Our partner was creating a life-changing gene therapy for treating Dystrophic Epidermolysis Bullosa (DEB), a rare and severe disease that affects the skin and mucosal tissues. The FDA granted the product orphan drug, fast … Read more